The US HHS has added Duchenne muscular dystrophy and metachromatic leukodystrophy to newborn screening, citing benefits of early detection and access to FDA-approved treatments.

Myotonic dystrophy type 1 (DM1) is the most common form of adult-onset muscular dystrophy, affecting about 1 in 8,000 people.

This announcement follows a bipartisan letter that Senator Collins and a group of nine members of Congress sent last month to ...

The Muscular Dystrophy Association (MDA) today announced more than $2.7 million in new research grants to advance groundbreaking discoveries across multiple neuromuscular diseases, including ...

Capricor stock skyrocketed to an eight-year high Wednesday, catapulting more than 300%, on positive results for its Duchenne muscular dystrophy treatment.The company is taking a cell therapy approach ...

In November 2025, Epicrispr Biotechnologies Inc. announced a clinical trial is to learn how safe and tolerable EPI-321 is and ...

Novartis had one eye on the struggles its peers have encountered in the muscular dystrophy space when it decided to acquire Kate Therapeutics, according to the Big Pharma’s CEO. The Swiss drugmaker ...

Muscular dystrophy is a group of conditions that damage and weaken your muscles over time. Symptoms, age of onset, and outlook depend on the type of muscular dystrophy you have. Muscular dystrophy ...

Macular retinal dystrophy is a rare genetic eye disorder that causes vision loss. Macular retinal dystrophy affects the back of your eye, or retina. It leads to cell damage in an area called the ...

Muscular dystrophy is a set of genetic diseases that cause muscles to become progressively weaker. Many forms of the disease ...

The FDA cited risk of IV infection and kidney toxicity in its letter. The company's CEO said the FDA issued no prior warning for the two concerns.

In the spirit of the holidays, we're looking back on the time the Grateful Dead played a surprise set for kids with muscular dystrophy.